Aartsma-Rus, Annemieke

Antisense-induced exon skipping for duplications in Duchenne muscular dystrophy. [electronic resource] - BMC medical genetics Jul 2007 - 43 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1471-2350

10.1186/1471-2350-8-43 doi


Cells, Cultured
Dystrophin--genetics
Exons
Gene Duplication
Gene Targeting
Genetic Therapy--methods
Humans
Muscle Fibers, Skeletal
Muscular Dystrophy, Duchenne--genetics
Oligonucleotides, Antisense--genetics
Reverse Transcriptase Polymerase Chain Reaction
Sequence Deletion