Wraith, J Edmond

Enzyme replacement therapy in patients who have mucopolysaccharidosis I and are younger than 5 years: results of a multinational study of recombinant human alpha-L-iduronidase (laronidase). [electronic resource] - Pediatrics Jul 2007 - e37-46 p. digital

Publication Type: Clinical Trial; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't

1098-4275

10.1542/peds.2006-2156 doi


Child Development
Child, Preschool
Female
Glycosaminoglycans--urine
Humans
Iduronidase--administration & dosage
Immunoglobulin G--blood
Infant
Infusions, Intravenous
Liver--pathology
Male
Mucopolysaccharidosis I--drug therapy
Recombinant Proteins--administration & dosage