Farah, Mohamed H
RNAi silencing in mouse models of neurodegenerative diseases. [electronic resource]
- Current drug delivery Apr 2007
- 161-7 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Review
1567-2018
10.2174/156720107780362276 doi
Alzheimer Disease--genetics
Amyloid Precursor Protein Secretases--genetics
Amyloidosis--genetics
Amyotrophic Lateral Sclerosis--genetics
Animals
Aspartic Acid Endopeptidases--genetics
Ataxin-1
Ataxins
Blood-Brain Barrier
Disease Models, Animal
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors
Huntingtin Protein
Huntington Disease--genetics
Mice
Nerve Tissue Proteins--genetics
Neurodegenerative Diseases--genetics
Nuclear Proteins--genetics
RNA Interference
RNA, Double-Stranded--genetics
RNA, Small Interfering--biosynthesis
Spinocerebellar Ataxias--genetics
Superoxide Dismutase--genetics
Superoxide Dismutase-1