Muenzer, Joseph
A phase I/II clinical trial of enzyme replacement therapy in mucopolysaccharidosis II (Hunter syndrome). [electronic resource]
- Molecular genetics and metabolism Mar 2007
- 329-37 p. digital
Publication Type: Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
ISSN: 1096-7192
Standard No.: 10.1016/j.ymgme.2006.09.001 doi
Subjects--Topical Terms: Adolescent Adult Child Double-Blind Method Glycosaminoglycans--urine Humans Iduronate Sulfatase--administration & dosage Immunoglobulin G--biosynthesis Infusions, Intravenous Joints--drug effects Liver--drug effects Male Mucopolysaccharidosis II--drug therapy Recombinant Proteins--administration & dosage Respiratory Function Tests Safety Spleen--drug effects