Muenzer, Joseph

A phase I/II clinical trial of enzyme replacement therapy in mucopolysaccharidosis II (Hunter syndrome). [electronic resource] - Molecular genetics and metabolism Mar 2007 - 329-37 p. digital

Publication Type: Clinical Trial, Phase I; Clinical Trial, Phase II; Journal Article; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

1096-7192

10.1016/j.ymgme.2006.09.001 doi


Adolescent
Adult
Child
Double-Blind Method
Glycosaminoglycans--urine
Humans
Iduronate Sulfatase--administration & dosage
Immunoglobulin G--biosynthesis
Infusions, Intravenous
Joints--drug effects
Liver--drug effects
Male
Mucopolysaccharidosis II--drug therapy
Recombinant Proteins--administration & dosage
Respiratory Function Tests
Safety
Spleen--drug effects