TY  - GEN
AU  - Broekman,M L D
AU  - Baek,R C
AU  - Comer,L A
AU  - Fernandez,J L
AU  - Seyfried,T N
AU  - Sena-Esteves,M
TI  - Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery
SN  - 1525-0024
PY  - 2008///0331
KW  - Animals
KW  - Animals, Newborn
KW  - Chromatography, High Pressure Liquid
KW  - Dependovirus
KW  - genetics
KW  - Gangliosidosis, GM1
KW  - enzymology
KW  - Genetic Therapy
KW  - Lipid Metabolism
KW  - Lysosomes
KW  - Mice
KW  - Mice, Inbred C57BL
KW  - Mice, Knockout
KW  - beta-Galactosidase
KW  - deficiency
N1  - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1038/sj.mt.6300004
ER  -