Broekman, M L D <br/><br/>
Complete correction of enzymatic deficiency and neurochemistry in the GM1-gangliosidosis mouse brain by neonatal adeno-associated virus-mediated gene delivery.  [electronic resource] 

 -  Molecular therapy : the journal of the American Society of Gene Therapy  Jan 2007 
 - 30-7 p.  digital 
<br/><br/> Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>1525-0024 
<br/><br/><label>Standard No.: </label>10.1038/sj.mt.6300004  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Animals<br/>Animals, Newborn<br/>Chromatography, High Pressure Liquid<br/>Dependovirus--genetics<br/>Gangliosidosis, GM1--enzymology<br/>Genetic Therapy<br/>Lipid Metabolism<br/>Lysosomes--enzymology<br/>Mice<br/>Mice, Inbred C57BL<br/>Mice, Knockout<br/>beta-Galactosidase--deficiency