Nathwani, Amit C

Safe and efficient transduction of the liver after peripheral vein infusion of self-complementary AAV vector results in stable therapeutic expression of human FIX in nonhuman primates. [electronic resource] - Blood Feb 2007 - 1414-21 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't

0006-4971

10.1182/blood-2006-03-010181 doi


Animals
Antibody Formation
Factor IX--administration & dosage
Genetic Therapy--methods
Genetic Vectors--administration & dosage
Hemophilia B--therapy
Humans
Liver--metabolism
Macaca
Tissue Distribution
Transduction, Genetic--methods
Treatment Outcome