Effects of transient immunosuppression on adenoassociated, virus-mediated, liver-directed gene transfer in rhesus macaques and implications for human gene therapy. [electronic resource]
- Blood Nov 2006
- 3321-8 p. digital
Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
0006-4971
10.1182/blood-2006-04-017913 doi
Animals Antibodies--pharmacology Dependovirus--genetics Drug Therapy, Combination Factor IX--administration & dosage Gene Transfer Techniques Genetic Therapy--methods Genetic Vectors--immunology Hemophilia B--therapy Humans Immunosuppression Therapy--methods Liver--metabolism Macaca mulatta Male Mice Mycophenolic Acid--administration & dosage Organ Specificity Tacrolimus--administration & dosage