Brooks, Doug A

Stop-codon read-through for patients affected by a lysosomal storage disorder. [electronic resource] - Trends in molecular medicine Aug 2006 - 367-73 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review

1471-4914

10.1016/j.molmed.2006.06.001 doi


Codon, Nonsense--genetics
Codon, Terminator--genetics
Gene Expression Regulation--drug effects
Gentamicins--therapeutic use
Humans
Lysosomal Storage Diseases--drug therapy
Models, Biological