Giraldo, Pilar

Short-term effect of miglustat in every day clinical use in treatment-naïve or previously treated patients with type 1 Gaucher's disease. [electronic resource] - Haematologica May 2006 - 703-6 p. digital

Publication Type: Clinical Trial; Comparative Study; Journal Article; Multicenter Study; Research Support, Non-U.S. Gov't

1592-8721


1-Deoxynojirimycin--administration & dosage
Administration, Oral
Adult
Aged
Bone Marrow--pathology
Chemokines, CC--blood
Drug Administration Schedule
Female
Gaucher Disease--drug therapy
Genotype
Glucosylceramidase--therapeutic use
Glucosylceramides--biosynthesis
Glucosyltransferases--antagonists & inhibitors
Hexosaminidases--blood
Humans
Male
Middle Aged
Neuropsychological Tests
Quality of Life
Treatment Outcome