Brichta, Lars

In vivo activation of SMN in spinal muscular atrophy carriers and patients treated with valproate. [electronic resource] - Annals of neurology Jun 2006 - 970-5 p. digital

Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't

0364-5134

10.1002/ana.20836 doi


Cyclic AMP Response Element-Binding Protein--blood
GABA Agents--therapeutic use
Gene Expression--drug effects
Heterozygote
Humans
Muscular Atrophy, Spinal--drug therapy
Nerve Tissue Proteins--blood
Pilot Projects
RNA, Messenger--blood
RNA-Binding Proteins--blood
SMN Complex Proteins
Survival of Motor Neuron 1 Protein
Survival of Motor Neuron 2 Protein
Valproic Acid--therapeutic use