TY - GEN AU - Sumner,C J AU - Kolb,S J AU - Harmison,G G AU - Jeffries,N O AU - Schadt,K AU - Finkel,R S AU - Dreyfuss,G AU - Fischbeck,K H TI - SMN mRNA and protein levels in peripheral blood: biomarkers for SMA clinical trials SN - 1526-632X PY - 2006///0502 KW - Biomarkers KW - blood KW - Cell Line KW - Clinical Trials as Topic KW - Cyclic AMP Response Element-Binding Protein KW - Genetic Carrier Screening KW - Humans KW - Infant KW - Lymphocytes KW - Muscular Atrophy, Spinal KW - Nerve Tissue Proteins KW - RNA, Messenger KW - RNA-Binding Proteins KW - Reference Values KW - SMN Complex Proteins KW - Survival of Motor Neuron 1 Protein KW - Survival of Motor Neuron 2 Protein N1 - Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, N.I.H., Intramural; Research Support, Non-U.S. Gov't UR - https://doi.org/10.1212/01.wnl.0000201929.56928.13 ER -