Paul, C A

Adenovirus expressing an NPC1-GFP fusion gene corrects neuronal and nonneuronal defects associated with Niemann pick type C disease. [electronic resource] - Journal of neuroscience research Sep 2005 - 706-19 p. digital

Publication Type: Comparative Study; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

0360-4012

10.1002/jnr.20592 doi


Adenoviridae--genetics
Animals
Astrocytes--metabolism
Biological Transport--physiology
Brain--metabolism
CHO Cells
Carrier Proteins--metabolism
Cholesterol--metabolism
Cricetinae
Female
Fibroblasts--metabolism
Genetic Techniques
Green Fluorescent Proteins--metabolism
Humans
Intracellular Signaling Peptides and Proteins
Membrane Glycoproteins--metabolism
Mice
Microscopy, Fluorescence
Neurons--metabolism
Niemann-Pick C1 Protein
Niemann-Pick Diseases--genetics
Ovary--cytology
Rats
Recombinant Fusion Proteins
Transduction, Genetic
Transfection