Osborn, Mark J

A picornaviral 2A-like sequence-based tricistronic vector allowing for high-level therapeutic gene expression coupled to a dual-reporter system. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy Sep 2005 - 569-74 p. digital

Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

1525-0016

10.1016/j.ymthe.2005.04.013 doi


Animals
Cysteine Endopeptidases--genetics
Gene Expression
Gene Transfer Techniques
Genes
Genes, Reporter
Genetic Therapy--methods
Genetic Vectors--genetics
Iduronidase--metabolism
In Vitro Techniques
Luciferases--metabolism
Luciferases, Firefly
Luminescent Proteins--genetics
Mice
Mice, Inbred NOD
Mice, SCID
Models, Genetic
Mucopolysaccharidoses--metabolism
NIH 3T3 Cells
Picornaviridae--genetics
Plasmids--metabolism
Protein Biosynthesis
Time Factors
Transfection
Viral Proteins--genetics