Grewal, Satkiran S

Safety and efficacy of enzyme replacement therapy in combination with hematopoietic stem cell transplantation in Hurler syndrome. [electronic resource] - Genetics in medicine : official journal of the American College of Medical Genetics Feb 2005 - 143-6 p. digital

Publication Type: Clinical Trial; Journal Article

1098-3600

10.1097/01.gim.0000154299.22120.6a doi


Acute Disease
Combined Modality Therapy
Female
Graft Rejection
Graft vs Host Disease
Hematopoietic Stem Cell Transplantation--adverse effects
Humans
Iduronidase--adverse effects
Infant
Male
Mucopolysaccharidosis I--drug therapy
Recombinant Proteins
Respiration, Artificial
Treatment Outcome