Aartsma-Rus, A <br/><br/>
Comparative analysis of antisense oligonucleotide analogs for targeted DMD exon 46 skipping in muscle cells.  [electronic resource] 

 -  Gene therapy  Sep 2004 
 - 1391-8 p.  digital 
<br/><br/> Publication Type: Comparative Study; Journal Article; Research Support, Non-U.S. Gov't 
<br/><br/><label>ISSN: </label>0969-7128 
<br/><br/><label>Standard No.: </label>10.1038/sj.gt.3302313  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Base Sequence<br/>Case-Control Studies<br/>Cells, Cultured<br/>Dystrophin--genetics<br/>Electrophoretic Mobility Shift Assay<br/>Exons<br/>Gene Dosage<br/>Genetic Therapy--methods<br/>Humans<br/>Molecular Sequence Data<br/>Muscle Cells--metabolism<br/>Muscle Fibers, Skeletal--metabolism<br/>Muscular Dystrophy, Duchenne--metabolism<br/>Oligonucleotides<br/>Oligonucleotides, Antisense--administration & dosage<br/>Sequence Alignment