Lau, Adeline A

In vitro characterization of genetically modified embryonic stem cells as a therapy for murine mucopolysaccharidosis type IIIA. [electronic resource] - Molecular genetics and metabolism Feb 2004 - 86-95 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1096-7192

10.1016/j.ymgme.2003.11.007 doi


Animals
CHO Cells
Cell Differentiation
Cell Line
Cricetinae
Cricetulus
Genetic Markers
Humans
Hydrolases--genetics
Mice
Mucopolysaccharidosis III--genetics
Recombinant Proteins--genetics
Stem Cells--cytology
Transfection