Harding, Cary O

Expression of phenylalanine hydroxylase (PAH) in erythrogenic bone marrow does not correct hyperphenylalaninemia in Pah(enu2) mice. [electronic resource] - The journal of gene medicine Nov 2003 - 984-93 p. digital

Publication Type: Comparative Study; Journal Article; Research Support, U.S. Gov't, P.H.S.

1099-498X

10.1002/jgm.432 doi


Animals
Animals, Genetically Modified
Biopterins--analogs & derivatives
Bone Marrow--metabolism
Chromatography, High Pressure Liquid
Crosses, Genetic
DNA, Complementary--genetics
Disease Models, Animal
Gene Expression
Globins--genetics
Humans
Luciferases
Mice
Phenylalanine Hydroxylase--genetics
Phenylketonurias--drug therapy
Promoter Regions, Genetic--genetics
Time Factors
Transfection
Transgenes--genetics