Brun, C

U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping. [electronic resource] - Cellular and molecular life sciences : CMLS Mar 2003 - 557-66 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

1420-682X

10.1007/s000180300047 doi


Animals
Dystrophin--metabolism
Exons
Genetic Therapy
Mice
Mice, Inbred mdx
Muscular Dystrophy, Duchenne--genetics
Mutation
RNA Precursors--metabolism
RNA Splicing--physiology
RNA, Antisense--metabolism
RNA, Small Nuclear--metabolism