Bertoni, Carmen

Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping. [electronic resource] - Human molecular genetics May 2003 - 1087-99 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

0964-6906

10.1093/hmg/ddg133 doi


Alternative Splicing
Animals
Base Sequence
Cytoskeletal Proteins--biosynthesis
Dystroglycans
Dystrophin--biosynthesis
Exons--genetics
Gene Expression Regulation
Membrane Glycoproteins--biosynthesis
Mice
Mice, Inbred mdx
Molecular Sequence Data
Muscle Cells--metabolism
Muscular Dystrophy, Duchenne--genetics
Oligodeoxyribonucleotides--metabolism
Oligoribonucleotides--genetics
Point Mutation