Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping. [electronic resource]
- Human molecular genetics May 2003
- 1087-99 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0964-6906
10.1093/hmg/ddg133 doi
Alternative Splicing Animals Base Sequence Cytoskeletal Proteins--biosynthesis Dystroglycans Dystrophin--biosynthesis Exons--genetics Gene Expression Regulation Membrane Glycoproteins--biosynthesis Mice Mice, Inbred mdx Molecular Sequence Data Muscle Cells--metabolism Muscular Dystrophy, Duchenne--genetics Oligodeoxyribonucleotides--metabolism Oligoribonucleotides--genetics Point Mutation