Jeyakumar, M

Glycosphingolipid lysosomal storage diseases: therapy and pathogenesis. [electronic resource] - Neuropathology and applied neurobiology Oct 2002 - 343-57 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review

0305-1846

10.1046/j.1365-2990.2002.00422.x doi


1-Deoxynojirimycin--administration & dosage
Animals
Bone Marrow Transplantation
Chemotherapy, Adjuvant
Disease Models, Animal
G(M2) Ganglioside--metabolism
Gangliosides--metabolism
Glucosylceramides--metabolism
Glucosyltransferases--antagonists & inhibitors
Glycosphingolipids--metabolism
Humans
Lysosomal Storage Diseases--etiology
Lysosomes--metabolism
Mice
Models, Biological
Models, Chemical
Morpholines--administration & dosage
Sandhoff Disease--etiology
Tay-Sachs Disease--etiology
Treatment Outcome