TY - GEN AU - Ponder,Katherine Parker AU - Melniczek,John R AU - Xu,Lingfei AU - Weil,Margaret A AU - O'Malley,Thomas M AU - O'Donnell,Patricia A AU - Knox,Van W AU - Aguirre,Gustavo D AU - Mazrier,Hamutal AU - Ellinwood,N Matthew AU - Sleeper,Meg AU - Maguire,Albert M AU - Volk,Susan W AU - Mango,Robert L AU - Zweigle,Jean AU - Wolfe,John H AU - Haskins,Mark E TI - Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs SN - 0027-8424 PY - 2002///1113 KW - Animals KW - Animals, Newborn KW - Dependovirus KW - genetics KW - Disease Models, Animal KW - Dogs KW - Eye KW - pathology KW - Female KW - Gene Transfer Techniques KW - Genetic Therapy KW - methods KW - Genetic Vectors KW - Hepatocyte Growth Factor KW - metabolism KW - Humans KW - Male KW - Mitral Valve KW - Mucopolysaccharidosis VII KW - embryology KW - Promoter Regions, Genetic KW - Receptor, IGF Type 2 KW - Time Factors KW - Tissue Distribution KW - alpha 1-Antitrypsin N1 - Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S UR - https://doi.org/10.1073/pnas.192353499 ER -