Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs. [electronic resource]
- Proceedings of the National Academy of Sciences of the United States of America Oct 2002
- 13102-7 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
0027-8424
10.1073/pnas.192353499 doi
Animals Animals, Newborn Dependovirus--genetics Disease Models, Animal Dogs Eye--pathology Female Gene Transfer Techniques Genetic Therapy--methods Genetic Vectors Hepatocyte Growth Factor--metabolism Humans Male Mitral Valve--pathology Mucopolysaccharidosis VII--embryology Promoter Regions, Genetic Receptor, IGF Type 2--metabolism Time Factors Tissue Distribution alpha 1-Antitrypsin--genetics