Ponder, Katherine Parker

Therapeutic neonatal hepatic gene therapy in mucopolysaccharidosis VII dogs. [electronic resource] - Proceedings of the National Academy of Sciences of the United States of America Oct 2002 - 13102-7 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

0027-8424

10.1073/pnas.192353499 doi


Animals
Animals, Newborn
Dependovirus--genetics
Disease Models, Animal
Dogs
Eye--pathology
Female
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors
Hepatocyte Growth Factor--metabolism
Humans
Male
Mitral Valve--pathology
Mucopolysaccharidosis VII--embryology
Promoter Regions, Genetic
Receptor, IGF Type 2--metabolism
Time Factors
Tissue Distribution
alpha 1-Antitrypsin--genetics