Kakkis, Emil D

Enzyme replacement therapy for the mucopolysaccharide storage disorders. [electronic resource] - Expert opinion on investigational drugs May 2002 - 675-85 p. digital

Publication Type: Journal Article; Review

1354-3784

10.1517/13543784.11.5.675 doi


Animals
Cats
Clinical Trials, Phase I as Topic
Clinical Trials, Phase II as Topic
Disease Models, Animal
Dogs
Humans
Iduronidase--therapeutic use
Mucopolysaccharidoses--drug therapy
Recombinant Proteins--therapeutic use
Treatment Outcome