Enzyme replacement therapy for the mucopolysaccharide storage disorders. [electronic resource]
- Expert opinion on investigational drugs May 2002
- 675-85 p. digital
Publication Type: Journal Article; Review
1354-3784
10.1517/13543784.11.5.675 doi
Animals Cats Clinical Trials, Phase I as Topic Clinical Trials, Phase II as Topic Disease Models, Animal Dogs Humans Iduronidase--therapeutic use Mucopolysaccharidoses--drug therapy Recombinant Proteins--therapeutic use Treatment Outcome