Elliger, Susan S

Enhanced secretion and uptake of beta-glucuronidase improves adeno-associated viral-mediated gene therapy of mucopolysaccharidosis type VII mice. [electronic resource] - Molecular therapy : the journal of the American Society of Gene Therapy May 2002 - 617-26 p. digital

Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.

1525-0016

10.1006/mthe.2002.0594 doi


Animals
Animals, Newborn--physiology
Blotting, Southern
Brain--enzymology
DNA Primers--chemistry
Dependovirus--genetics
Gene Expression
Gene Transfer Techniques
Genetic Therapy--methods
Genetic Vectors
Glucuronidase--genetics
Heterozygote
Homozygote
Humans
Liver--enzymology
Mice
Mice, Inbred C57BL
Mice, Knockout
Mice, Transgenic
Mucopolysaccharidosis VII--enzymology
Reverse Transcriptase Polymerase Chain Reaction
Spleen--enzymology
Tissue Distribution