Hammerhead ribozymes designed to cleave all human rod opsin mRNAs which cause autosomal dominant retinitis pigmentosa. [electronic resource]
- Molecular vision Apr 2002
- 102-13 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
1090-0535
Base Sequence Drug Design Electrophoresis, Polyacrylamide Gel Formamides--pharmacology Gene Expression Hot Temperature Humans Immunohistochemistry Molecular Sequence Data Plasmids Polymerase Chain Reaction RNA--metabolism RNA, Catalytic--genetics RNA, Messenger--metabolism Retinal Rod Photoreceptor Cells--drug effects Retinitis Pigmentosa--genetics Rod Opsins--genetics Transcription, Genetic Transfection