Mode of action of RNA/DNA oligonucleotides: progress in the development of gene repair as a therapy for alpha(1)-antitrypsin deficiency. [electronic resource]
- Chest Mar 2002
- 91S-97S p. digital
Publication Type: Journal Article
0012-3692
10.1378/chest.121.3_suppl.91s doi
Adenosine Triphosphatases Bacterial Proteins--genetics DNA Repair DNA-Binding Proteins Escherichia coli Proteins Genetic Therapy Humans MutS DNA Mismatch-Binding Protein Mutagenesis, Site-Directed Phenotype Pulmonary Emphysema--etiology Rec A Recombinases--genetics Structure-Activity Relationship alpha 1-Antitrypsin--genetics alpha 1-Antitrypsin Deficiency--complications