Leone, P <br/><br/>
Global CNS gene transfer for a childhood neurogenetic enzyme deficiency: Canavan disease.  [electronic resource] 

 -  Current opinion in molecular therapeutics  Aug 1999 
 - 487-92 p.  digital 
<br/><br/> Publication Type: Journal Article; Review 
<br/><br/><label>ISSN: </label>1464-8431 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Acetates--therapeutic use<br/>Acetazolamide--therapeutic use<br/>Amidohydrolases--deficiency<br/>Animals<br/>Aspartic Acid--analogs & derivatives<br/>Brain--enzymology<br/>Brain Edema--etiology<br/>Calcium Compounds<br/>Canavan Disease--diagnosis<br/>Child<br/>Child, Preschool<br/>Cholesterol--administration & dosage<br/>Combined Modality Therapy<br/>Cytomegalovirus--genetics<br/>DNA, Recombinant--administration & dosage<br/>Dependovirus--genetics<br/>Female<br/>Fetal Diseases--diagnosis<br/>Genetic Therapy<br/>Genetic Vectors--administration & dosage<br/>Glycerophospholipids--administration & dosage<br/>Humans<br/>Infant<br/>Injections, Intraventricular<br/>Liposomes--administration & dosage<br/>Male<br/>Mitochondria--metabolism<br/>Nerve Tissue Proteins--deficiency<br/>Osmotic Pressure<br/>Phosphatidylethanolamines<br/>Prenatal Diagnosis<br/>Primates<br/>Promoter Regions, Genetic<br/>Protamines--administration & dosage<br/>Rats