Roth, D A Nonviral transfer of the gene encoding coagulation factor VIII in patients with severe hemophilia A. [electronic resource] - The New England journal of medicine Jun 2001 - 1735-42 p. digital Publication Type: Clinical Trial; Clinical Trial, Phase I; Journal Article; Research Support, Non-U.S. Gov't ISSN: 0028-4793 Standard No.: 10.1056/NEJM200106073442301 doi Subjects--Topical Terms: AdultAgedBiopsyClone CellsFactor VIII--geneticsFibroblasts--transplantationGenetic Therapy--methodsHemophilia A--geneticsHemorrhage--epidemiologyHumansLaparoscopyMiddle AgedOmentumPlasmids--geneticsSkin--cytologyTransfection--methodsTransplantation, Autologous