Nonablative neonatal marrow transplantation attenuates functional and physical defects of beta-glucuronidase deficiency. [electronic resource]
- Blood Mar 2001
- 1498-504 p. digital
Publication Type: Evaluation Study; Journal Article; Research Support, U.S. Gov't, P.H.S.
0006-4971
10.1182/blood.v97.5.1498 doi
Adult Animals Animals, Newborn Bone Marrow Transplantation--methods Female Femur--abnormalities Glucuronidase--deficiency Graft Survival Humans Male Mice Mice, Inbred BALB C Mice, Mutant Strains Mucopolysaccharidosis VII--therapy Reproduction Tissue Distribution