Factors influencing in vivo transduction by recombinant adeno-associated viral vectors expressing the human factor IX cDNA. [electronic resource]
- Blood Mar 2001
- 1258-65 p. digital
Publication Type: Comparative Study; Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
0006-4971
10.1182/blood.v97.5.1258 doi
Animals Antibodies--analysis DNA, Complementary--pharmacokinetics DNA, Recombinant Dependovirus--genetics Factor IX--genetics Genetic Vectors--administration & dosage Humans Injections, Intramuscular Injections, Intravenous Male Mice Mice, Inbred BALB C Mice, Inbred C57BL Mice, SCID Portal Vein Time Factors Tissue Distribution Transduction, Genetic--methods