Kakkis, E D <br/><br/>
Enzyme-replacement therapy in mucopolysaccharidosis I.  [electronic resource] 

 -  The New England journal of medicine  Jan 2001 
 - 182-8 p.  digital 
<br/><br/> Publication Type: Clinical Trial; Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S. 
<br/><br/><label>ISSN: </label>0028-4793 
<br/><br/><label>Standard No.: </label>10.1056/NEJM200101183440304  doi 
<br/><br/><label>Subjects--Topical Terms: </label><br/>Adolescent<br/>Adult<br/>Apnea--drug therapy<br/>Child<br/>Child, Preschool<br/>Corneal Opacity--drug therapy<br/>Exercise Tolerance--drug effects<br/>Female<br/>Growth--drug effects<br/>Hepatomegaly--drug therapy<br/>Humans<br/>Iduronidase--adverse effects<br/>Infusions, Intravenous<br/>Male<br/>Mucopolysaccharidosis I--complications<br/>Range of Motion, Articular--drug effects<br/>Splenomegaly--drug therapy