TY  - GEN
AU  - Jeyakumar,M
AU  - Norflus,F
AU  - Tifft,C J
AU  - Cortina-Borja,M
AU  - Butters,T D
AU  - Proia,R L
AU  - Perry,V H
AU  - Dwek,R A
AU  - Platt,F M
TI  - Enhanced survival in Sandhoff disease mice receiving a combination of substrate deprivation therapy and bone marrow transplantation
SN  - 0006-4971
PY  - 2001///0215
KW  - 1-Deoxynojirimycin
KW  - analogs & derivatives
KW  - Animals
KW  - Bone Marrow Transplantation
KW  - Brain
KW  - metabolism
KW  - Diagnostic Techniques, Neurological
KW  - Disease Models, Animal
KW  - Enzyme Inhibitors
KW  - therapeutic use
KW  - Glycosphingolipids
KW  - Hexosaminidase B
KW  - Mice
KW  - Sandhoff Disease
KW  - therapy
KW  - Spinal Cord
KW  - Survival Rate
KW  - beta-N-Acetylhexosaminidases
N1  - Publication Type: Journal Article; Research Support, Non-U.S. Gov't
UR  - https://doi.org/10.1182/blood.v97.1.327
ER  -