Jeyakumar, M

Enhanced survival in Sandhoff disease mice receiving a combination of substrate deprivation therapy and bone marrow transplantation. [electronic resource] - Blood Jan 2001 - 327-9 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't

0006-4971

10.1182/blood.v97.1.327 doi


1-Deoxynojirimycin--analogs & derivatives
Animals
Bone Marrow Transplantation
Brain--metabolism
Diagnostic Techniques, Neurological
Disease Models, Animal
Enzyme Inhibitors--therapeutic use
Glycosphingolipids--metabolism
Hexosaminidase B
Mice
Sandhoff Disease--therapy
Spinal Cord--metabolism
Survival Rate
beta-N-Acetylhexosaminidases--metabolism