Enhanced survival in Sandhoff disease mice receiving a combination of substrate deprivation therapy and bone marrow transplantation. [electronic resource]
- Blood Jan 2001
- 327-9 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
0006-4971
10.1182/blood.v97.1.327 doi
1-Deoxynojirimycin--analogs & derivatives Animals Bone Marrow Transplantation Brain--metabolism Diagnostic Techniques, Neurological Disease Models, Animal Enzyme Inhibitors--therapeutic use Glycosphingolipids--metabolism Hexosaminidase B Mice Sandhoff Disease--therapy Spinal Cord--metabolism Survival Rate beta-N-Acetylhexosaminidases--metabolism