Owen R, I V
Recombinant adeno-associated virus vector-based gene transfer for defects in oxidative metabolism. [electronic resource]
- Human gene therapy Oct 2000
- 2067-78 p. digital
Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.
ISSN: 1043-0342
Standard No.: 10.1089/104303400750001381 doi
Subjects--Topical Terms: Acidosis, Lactic--congenital Adenosine Triphosphatases--metabolism Animals Cell Line Cell Nucleus--metabolism DNA, Mitochondrial--genetics Dependovirus--genetics Gene Transfer Techniques Genes, Reporter Genetic Therapy--methods Genetic Vectors Green Fluorescent Proteins Humans Luminescent Proteins--biosynthesis Microscopy, Fluorescence Mitochondria--metabolism Mitochondrial Proton-Translocating ATPases Models, Genetic Mutation Neurons--metabolism Oxygen--metabolism Pyruvate Dehydrogenase Complex--chemistry Pyruvate Dehydrogenase Complex Deficiency Disease Rats Recombinant Fusion Proteins--metabolism Spinal Cord--metabolism Transduction, Genetic Transfection Tumor Cells, Cultured