Owen R, I V

Recombinant adeno-associated virus vector-based gene transfer for defects in oxidative metabolism. [electronic resource] - Human gene therapy Oct 2000 - 2067-78 p. digital

Publication Type: Journal Article; Research Support, U.S. Gov't, P.H.S.

1043-0342

10.1089/104303400750001381 doi


Acidosis, Lactic--congenital
Adenosine Triphosphatases--metabolism
Animals
Cell Line
Cell Nucleus--metabolism
DNA, Mitochondrial--genetics
Dependovirus--genetics
Gene Transfer Techniques
Genes, Reporter
Genetic Therapy--methods
Genetic Vectors
Green Fluorescent Proteins
Humans
Luminescent Proteins--biosynthesis
Microscopy, Fluorescence
Mitochondria--metabolism
Mitochondrial Proton-Translocating ATPases
Models, Genetic
Mutation
Neurons--metabolism
Oxygen--metabolism
Pyruvate Dehydrogenase Complex--chemistry
Pyruvate Dehydrogenase Complex Deficiency Disease
Rats
Recombinant Fusion Proteins--metabolism
Spinal Cord--metabolism
Transduction, Genetic
Transfection
Tumor Cells, Cultured