Pawliuk, R

Long-term cure of the photosensitivity of murine erythropoietic protoporphyria by preselective gene therapy. [electronic resource] - Nature medicine Jul 1999 - 768-73 p. digital

Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.

1078-8956

10.1038/10488 doi


Animals
Bone Marrow Transplantation
Erythrocytes--metabolism
Ferrochelatase--biosynthesis
Gene Transfer Techniques
Genetic Therapy
Green Fluorescent Proteins
Hematopoietic Stem Cells
Humans
Luminescent Proteins--biosynthesis
Male
Mice
Mice, Inbred BALB C
Photosensitivity Disorders--blood
Porphyria, Hepatoerythropoietic--blood
Protoporphyria, Erythropoietic
Protoporphyrins--blood
Skin--pathology
Transplantation, Isogeneic