Long-term cure of the photosensitivity of murine erythropoietic protoporphyria by preselective gene therapy. [electronic resource]
- Nature medicine Jul 1999
- 768-73 p. digital
Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
1078-8956
10.1038/10488 doi
Animals Bone Marrow Transplantation Erythrocytes--metabolism Ferrochelatase--biosynthesis Gene Transfer Techniques Genetic Therapy Green Fluorescent Proteins Hematopoietic Stem Cells Humans Luminescent Proteins--biosynthesis Male Mice Mice, Inbred BALB C Photosensitivity Disorders--blood Porphyria, Hepatoerythropoietic--blood Protoporphyria, Erythropoietic Protoporphyrins--blood Skin--pathology Transplantation, Isogeneic