Gene therapy for severe combined immunodeficiency caused by adenosine deaminase deficiency: improved retroviral vectors for clinical trials. [electronic resource]
- Acta haematologica 1999
- 89-96 p. digital
Publication Type: Journal Article; Review
0001-5792
10.1159/000040930 doi
Adenosine Deaminase--deficiency Animals Clinical Trials as Topic Genetic Therapy Genetic Vectors Humans Retroviridae--genetics Severe Combined Immunodeficiency--enzymology