A demonstration using mouse models that successful gene therapy for cystic fibrosis requires only partial gene correction. [electronic resource]
Producer: 19970108Description: 797-801 p. digitalISSN:- 0969-7128
- Animals
- Chlorides -- metabolism
- Colforsin -- pharmacology
- Crosses, Genetic
- Cystic Fibrosis -- metabolism
- Cystic Fibrosis Transmembrane Conductance Regulator -- genetics
- Electric Conductivity
- Gene Expression
- Genes, Recessive -- genetics
- Genetic Therapy -- methods
- Genotype
- Intestines -- chemistry
- Mice
- Mice, Mutant Strains
- Phenotype
- RNA, Messenger -- analysis
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Publication Type: Journal Article; Research Support, Non-U.S. Gov't
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