Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial. [electronic resource]
Producer: 20191206Description: 1940-1948 p. digitalISSN:- 1474-547X
- Adolescent
- Aminophenols -- administration & dosage
- Benzodioxoles -- administration & dosage
- Child
- Chloride Channel Agonists -- administration & dosage
- Cystic Fibrosis -- drug therapy
- Cystic Fibrosis Transmembrane Conductance Regulator -- genetics
- Double-Blind Method
- Drug Therapy, Combination
- Female
- Humans
- Indoles -- administration & dosage
- Male
- Pyrazoles -- administration & dosage
- Pyridines -- administration & dosage
- Pyrrolidines -- administration & dosage
- Quinolones -- administration & dosage
- Sweat -- chemistry
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Publication Type: Clinical Trial, Phase III; Journal Article; Randomized Controlled Trial; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
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