A Novel AAV-mediated Gene Delivery System Corrects CFTR Function in Pigs. [electronic resource]
Producer: 20200424Description: 747-754 p. digitalISSN:- 1535-4989
- Animals
- Animals, Newborn
- Cystic Fibrosis -- genetics
- Cystic Fibrosis Transmembrane Conductance Regulator -- administration & dosage
- DNA Transposable Elements
- Dependovirus -- genetics
- Gene Knockout Techniques
- Genes, Synthetic
- Genetic Therapy
- Genetic Vectors -- therapeutic use
- Humans
- Promoter Regions, Genetic
- Staphylococcus aureus
- Swine
- Trachea -- metabolism
- Virus Integration
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Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
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