Risdiplam distributes and increases SMN protein in both the central nervous system and peripheral organs. [electronic resource]
Producer: 20190204Description: e00447 p. digitalISSN:- 2052-1707
- Animals
- Azo Compounds -- cerebrospinal fluid
- Brain -- metabolism
- Clinical Trials as Topic
- Disease Models, Animal
- Dogs
- Drug Evaluation, Preclinical
- Exons -- drug effects
- Female
- Humans
- Macaca fascicularis
- Madin Darby Canine Kidney Cells
- Male
- Mice
- Muscular Atrophy, Spinal -- drug therapy
- Neuromuscular Agents -- cerebrospinal fluid
- Pyrimidines -- cerebrospinal fluid
- RNA Splicing -- drug effects
- Rats
- Rats, Wistar
- Survival of Motor Neuron 1 Protein -- metabolism
- Survival of Motor Neuron 2 Protein -- genetics
- Swine
- Tissue Distribution
No physical items for this record
Publication Type: Journal Article; Research Support, Non-U.S. Gov't
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