Site-Specific Gene Editing of Human Hematopoietic Stem Cells for X-Linked Hyper-IgM Syndrome. [electronic resource]
Producer: 20191105Description: 2606-2616 p. digitalISSN:- 2211-1247
- Animals
- Antigens, CD34 -- metabolism
- Base Sequence
- CD40 Ligand -- metabolism
- CRISPR-Associated Protein 9 -- metabolism
- CRISPR-Cas Systems -- genetics
- Cell Differentiation
- Cell Line
- Colony-Forming Units Assay
- DNA Repair
- DNA, Complementary -- genetics
- Gene Editing
- Genetic Diseases, X-Linked -- genetics
- Hematopoietic Stem Cells -- metabolism
- Humans
- Hyper-IgM Immunodeficiency Syndrome -- genetics
- Mice
- T-Lymphocytes -- metabolism
- Transcription Activator-Like Effector Nucleases -- metabolism
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Publication Type: Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't
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