In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy. [electronic resource]
Producer: 20170606Description: 1247-57 p. digitalISSN:- 1525-0024
- Animals
- Capsid Proteins -- chemistry
- Central Nervous System -- metabolism
- Dependovirus -- classification
- Gene Expression
- Gene Transfer Techniques
- Genes, Reporter
- Genetic Therapy
- Genetic Vectors -- administration & dosage
- Humans
- Mice
- Models, Molecular
- Muscles -- metabolism
- Protein Conformation
- Transduction, Genetic
- Transgenes
- Viral Tropism
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Publication Type: Journal Article; Research Support, N.I.H., Extramural
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