Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotype. [electronic resource]
Producer: 20170921Description: 2633-2644 p. digitalISSN:- 1460-2083
- Animals
- Dystrophin -- genetics
- Gene Expression
- Gene Transfer Techniques
- Genetic Therapy -- methods
- Genetic Vectors
- Genomics
- Mice
- Mice, Inbred CBA
- Mice, Inbred mdx
- Mice, Transgenic
- Muscle, Skeletal -- metabolism
- Muscular Dystrophy, Animal -- genetics
- Muscular Dystrophy, Duchenne -- genetics
- Myocardium -- metabolism
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Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Research Support, N.I.H., Extramural; Research Support, U.S. Gov't, Non-P.H.S.
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