Restoration of CFTR function in patients with cystic fibrosis carrying the F508del-CFTR mutation. [electronic resource]
Producer: 20150914Description: 2053-74 p. digitalISSN:- 1554-8635
- Adaptor Proteins, Signal Transducing -- metabolism
- Administration, Oral
- Adolescent
- Adult
- Animals
- Apoptosis Regulatory Proteins -- metabolism
- Beclin-1
- Catechin -- analogs & derivatives
- Cell Membrane -- metabolism
- Child
- Chlorides -- chemistry
- Cystamine -- pharmacology
- Cysteamine -- administration & dosage
- Cystic Fibrosis -- metabolism
- Cystic Fibrosis Transmembrane Conductance Regulator -- genetics
- Female
- Homozygote
- Humans
- Interleukin-8 -- metabolism
- Male
- Membrane Proteins -- metabolism
- Mice
- Mice, Inbred CFTR
- Mice, Transgenic
- Mutation
- Phenotype
- Pilot Projects
- Sequestosome-1 Protein
- Tumor Necrosis Factor-alpha -- metabolism
- Young Adult
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Publication Type: Clinical Trial, Phase II; Journal Article; Research Support, Non-U.S. Gov't
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