Phase I trial of intranasal and endobronchial administration of a recombinant adeno-associated virus serotype 2 (rAAV2)-CFTR vector in adult cystic fibrosis patients: a two-part clinical study. [electronic resource]
Producer: 20030926Description: 1079-88 p. digitalISSN:- 1043-0342
- Administration, Intranasal
- Adolescent
- Adult
- Antibodies, Viral -- blood
- Bronchi
- Cystic Fibrosis -- diagnosis
- Cystic Fibrosis Transmembrane Conductance Regulator -- genetics
- DNA, Recombinant -- genetics
- DNA, Viral -- analysis
- Dependovirus -- genetics
- Enzyme-Linked Immunosorbent Assay
- Genetic Vectors -- administration & dosage
- Humans
- Interleukins -- biosynthesis
- Male
- Viremia -- diagnosis
- Virus Shedding
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Publication Type: Clinical Trial; Clinical Trial, Phase I; Journal Article; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S.
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