Glycosphingolipid lysosomal storage diseases: therapy and pathogenesis. [electronic resource]
Producer: 20030312Description: 343-57 p. digitalISSN:- 0305-1846
- 1-Deoxynojirimycin -- administration & dosage
- Animals
- Bone Marrow Transplantation
- Chemotherapy, Adjuvant
- Disease Models, Animal
- G(M2) Ganglioside -- metabolism
- Gangliosides -- metabolism
- Glucosylceramides -- metabolism
- Glucosyltransferases -- antagonists & inhibitors
- Glycosphingolipids -- metabolism
- Humans
- Lysosomal Storage Diseases -- etiology
- Lysosomes -- metabolism
- Mice
- Models, Biological
- Models, Chemical
- Morpholines -- administration & dosage
- Sandhoff Disease -- etiology
- Tay-Sachs Disease -- etiology
- Treatment Outcome
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Publication Type: Journal Article; Research Support, Non-U.S. Gov't; Review
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