Global CNS gene transfer for a childhood neurogenetic enzyme deficiency: Canavan disease. [electronic resource]
Producer: 20020102Description: 487-92 p. digitalISSN:- 1464-8431
- Acetates -- therapeutic use
- Acetazolamide -- therapeutic use
- Amidohydrolases -- deficiency
- Animals
- Aspartic Acid -- analogs & derivatives
- Brain -- enzymology
- Brain Edema -- etiology
- Calcium Compounds
- Canavan Disease -- diagnosis
- Child
- Child, Preschool
- Cholesterol -- administration & dosage
- Combined Modality Therapy
- Cytomegalovirus -- genetics
- DNA, Recombinant -- administration & dosage
- Dependovirus -- genetics
- Female
- Fetal Diseases -- diagnosis
- Genetic Therapy
- Genetic Vectors -- administration & dosage
- Glycerophospholipids -- administration & dosage
- Humans
- Infant
- Injections, Intraventricular
- Liposomes -- administration & dosage
- Male
- Mitochondria -- metabolism
- Nerve Tissue Proteins -- deficiency
- Osmotic Pressure
- Phosphatidylethanolamines
- Prenatal Diagnosis
- Primates
- Promoter Regions, Genetic
- Protamines -- administration & dosage
- Rats
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Publication Type: Journal Article; Review
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