Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study. (Record no. 30575806)
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| 000 -LEADER | |
|---|---|
| fixed length control field | 01681 a2200445 4500 |
| 005 - DATE AND TIME OF LATEST TRANSACTION | |
| control field | 20250518082904.0 |
| 008 - FIXED-LENGTH DATA ELEMENTS--GENERAL INFORMATION | |
| fixed length control field | 202104s 0 0 eng d |
| 022 ## - INTERNATIONAL STANDARD SERIAL NUMBER | |
| International Standard Serial Number | 2042-6313 |
| 024 7# - OTHER STANDARD IDENTIFIER | |
| Standard number or code | 10.2217/cer-2019-0171 |
| Source of number or code | doi |
| 040 ## - CATALOGING SOURCE | |
| Original cataloging agency | NLM |
| Language of cataloging | eng |
| Transcribing agency | NLM |
| 100 1# - MAIN ENTRY--PERSONAL NAME | |
| Personal name | Mercuri, Eugenio |
| 264 #0 - PRODUCTION, PUBLICATION, DISTRIBUTION, MANUFACTURE, AND COPYRIGHT NOTICE | |
| Date of production, publication, distribution, manufacture, or copyright notice | 20210401 |
| 245 00 - TITLE STATEMENT | |
| Title | Safety and effectiveness of ataluren: comparison of results from the STRIDE Registry and CINRG DMD Natural History Study. |
| Medium | [electronic resource] |
| 260 ## - PUBLICATION, DISTRIBUTION, ETC. | |
| Name of publisher, distributor, etc. | Journal of comparative effectiveness research |
| Date of publication, distribution, etc. | 04 2020 |
| 300 ## - PHYSICAL DESCRIPTION | |
| Extent | 341-360 p. |
| Other physical details | digital |
| 500 ## - GENERAL NOTE | |
| General note | Publication Type: Journal Article; Multicenter Study; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, Non-P.H.S. |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Codon, Nonsense |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Dystrophin |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Humans |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Muscular Dystrophy, Duchenne |
| General subdivision | drug therapy |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Oxadiazoles |
| General subdivision | adverse effects |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Registries |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Treatment Outcome |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Muntoni, Francesco |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Osorio, Andrés Nascimento |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Tulinius, Már |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Buccella, Filippo |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Morgenroth, Lauren P |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Gordish-Dressman, Heather |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Jiang, Joel |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Trifillis, Panayiota |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Zhu, Jin |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Kristensen, Allan |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Santos, Claudio L |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Henricson, Erik K |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | McDonald, Craig M |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Desguerre, Isabelle |
| 773 0# - HOST ITEM ENTRY | |
| Title | Journal of comparative effectiveness research |
| Related parts | vol. 9 |
| -- | no. 5 |
| -- | p. 341-360 |
| 856 40 - ELECTRONIC LOCATION AND ACCESS | |
| Uniform Resource Identifier | <a href="https://doi.org/10.2217/cer-2019-0171">https://doi.org/10.2217/cer-2019-0171</a> |
| Public note | Available from publisher's website |
No items available.