Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy. (Record no. 23377539)
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| 000 -LEADER | |
|---|---|
| fixed length control field | 01438 a2200397 4500 |
| 005 - DATE AND TIME OF LATEST TRANSACTION | |
| control field | 20250516185431.0 |
| 008 - FIXED-LENGTH DATA ELEMENTS--GENERAL INFORMATION | |
| fixed length control field | 201409s 0 0 eng d |
| 022 ## - INTERNATIONAL STANDARD SERIAL NUMBER | |
| International Standard Serial Number | 1932-6203 |
| 024 7# - OTHER STANDARD IDENTIFIER | |
| Standard number or code | 10.1371/journal.pone.0081302 |
| Source of number or code | doi |
| 040 ## - CATALOGING SOURCE | |
| Original cataloging agency | NLM |
| Language of cataloging | eng |
| Transcribing agency | NLM |
| 100 1# - MAIN ENTRY--PERSONAL NAME | |
| Personal name | Finkel, Richard S |
| 264 #0 - PRODUCTION, PUBLICATION, DISTRIBUTION, MANUFACTURE, AND COPYRIGHT NOTICE | |
| Date of production, publication, distribution, manufacture, or copyright notice | 20140925 |
| 245 00 - TITLE STATEMENT | |
| Title | Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy. |
| Medium | [electronic resource] |
| 260 ## - PUBLICATION, DISTRIBUTION, ETC. | |
| Name of publisher, distributor, etc. | PloS one |
| Date of publication, distribution, etc. | 2013 |
| 300 ## - PHYSICAL DESCRIPTION | |
| Extent | e81302 p. |
| Other physical details | digital |
| 500 ## - GENERAL NOTE | |
| General note | Publication Type: Clinical Trial, Phase II; Journal Article; Research Support, N.I.H., Extramural; Research Support, Non-U.S. Gov't; Research Support, U.S. Gov't, P.H.S. |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Child |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Codon, Nonsense |
| General subdivision | genetics |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Dystrophin |
| General subdivision | metabolism |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Humans |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Male |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Muscular Dystrophy, Duchenne |
| General subdivision | drug therapy |
| 650 04 - SUBJECT ADDED ENTRY--TOPICAL TERM | |
| Topical term or geographic name entry element | Oxadiazoles |
| General subdivision | therapeutic use |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Flanigan, Kevin M |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Wong, Brenda |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Bönnemann, Carsten |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Sampson, Jacinda |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Sweeney, H Lee |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Reha, Allen |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Northcutt, Valerie J |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Elfring, Gary |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Barth, Jay |
| 700 1# - ADDED ENTRY--PERSONAL NAME | |
| Personal name | Peltz, Stuart W |
| 773 0# - HOST ITEM ENTRY | |
| Title | PloS one |
| Related parts | vol. 8 |
| -- | no. 12 |
| -- | p. e81302 |
| 856 40 - ELECTRONIC LOCATION AND ACCESS | |
| Uniform Resource Identifier | <a href="https://doi.org/10.1371/journal.pone.0081302">https://doi.org/10.1371/journal.pone.0081302</a> |
| Public note | Available from publisher's website |
No items available.